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Rare Diseases

A rare disease is a condition that affects fewer than 200,000 people. There are as many as 7,000 identified rare diseases, which affects an estimated 25-30 million Americans. Due to their nature, little is known about most rare diseases, and they are often misdiagnosed or late to diagnose.

COUR’s Rare Diseases Programs

  • CNP-104 (Primary Biliary Cholangitis)
  • CNP-106 (Myasthenia Gravis)
  • CNP-105 (Immune Thrombocytopenia Purpura)

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